Trial intelligence / Profile preview

ENVISION phase 3 study of delandistrogene moxeparvovec in Duchenne muscular dystrophy

2024-512626-28-00Phase 3Suspended

Sponsor
Sarepta Therapeutics
Start
Feb 2024
Modality
Gene Therapies
Countries
15
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Overview

Phase 3, randomised, double-blind trial in Duchenne muscular dystrophy (DMD) comparing Delandistrogene moxeparvovec with Placebo (2 arms). Primary endpoint: Change from baseline in total Performance of Upper Limb score. Started Feb 2024; status: suspended.

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Drugs

delandistrogene moxeparvovec
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Conditions

Duchenne muscular dystrophy (DMD)

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