Study design & results
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Trial intelligence / Profile preview
Avalglucosidase Alfa in Treatment-naïve Infantile-Onset Pompe Disease
2024-513859-33-00Phase 3Completed
- Sponsor
- Sanofi
- Start
- Jul 2024
- Modality
- Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
- Countries
- 9
01
Overview
Phase 3, open-label, single-arm trial of avalglucosidase alfa in Pompe disease, sponsored by Sanofi. Started Jul 2024; status: completed.
02
Drugs
avalglucosidase alfa
03
Conditions
Pompe disease
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Study design, results and competitive context are available in the Gosset platform where reported.
Competitive context
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