Trial intelligence / Profile preview

Effectiveness of ambroxol in children and adults with Gaucher disease 3: n-of-1 series

2024-514012-28-00Phase 3Authorised

Sponsor
Amsterdam University Medical Center
Start
Nov 2024
Modality
Small Molecules
Countries
1
01

Overview

Phase 3, open-label, single-arm trial of ambroxol in Gaucher disease type 3, sponsored by Amsterdam University Medical Center. Planned start Nov 2024; status: authorised.

02

Drugs

ambroxol
03

Conditions

Gaucher disease type 3

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