Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
ORION-20 inclisiran in children with heterozygous familial hypercholesterolemia
2024-514594-21-00Phase 3Authorised
- Sponsor
- Novartis
- Start
- Mar 2025
- Modality
- Chemically Modified siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Conjugated siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, MicroRNA (miRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
- Countries
- 23
01
Overview
Phase 3, randomised, double-blind trial in familial hypercholesterolemia (FH) comparing Inclisiran arm with Placebo then inclisiran arm (2 arms). Planned start Mar 2025; status: authorised.
02
Drugs
inclisiran
03
Conditions
familial hypercholesterolemia (FH)
Beyond the preview
Go deeper on 2024-514594-21-00.
Study design, results and competitive context are available in the Gosset platform where reported.
Competitive context
Available in the Gosset platform where reported.
Bring the full picture into focus.
See how Gosset can support your research on 2024-514594-21-00.