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Trial intelligence / Profile preview
French multicenter long-term extension study of avalglucosidase alfa in Pompe disease
2024-514773-22-00Phase 4Authorised
- Sponsor
- Sanofi
- Start
- Aug 2024
- Modality
- Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
- Countries
- 1
01
Overview
Phase 4, open-label, single-arm trial of avalglucosidase alfa in Pompe disease, sponsored by Sanofi. Primary endpoint: Number of adverse events and treatment-emergent adverse events. Planned start Aug 2024; status: authorised.
02
Drugs
avalglucosidase alfa
03
Conditions
Pompe disease
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Study design, results and competitive context are available in the Gosset platform where reported.
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