Trial intelligence / Profile preview

Phase 2a study of VX-407 in autosomal dominant polycystic kidney disease with selected PKD1 variants

2024-517393-13-00Phase 2Authorised

Sponsor
Vertex Pharmaceuticals
Start
Dec 2025
Modality
Small Molecules
Countries
9
01

Overview

Phase 2, open-label, single-arm trial of VX-407 in autosomal dominant polycystic kidney disease (ADPKD), sponsored by Vertex Pharmaceuticals. Primary endpoint: Proportion of subjects with non-increase in htTKV over time. Planned start Dec 2025; status: authorised.

02

Drugs

VX-407
03

Conditions

autosomal dominant polycystic kidney disease (ADPKD)

Beyond the preview

Go deeper on 2024-517393-13-00.

Study design, results and competitive context are available in the Gosset platform where reported.

Study design & results

Available in the Gosset platform where reported.

Competitive context

Available in the Gosset platform where reported.

Bring the full picture into focus.

See how Gosset can support your research on 2024-517393-13-00.

Gosset Free

Get started with Gosset.

Enter your corporate email.

Work email preferred.

Book a call