Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
Long-term safety study of personalized cholic acid treatment in bile acid synthesis defects
2024-518652-23-00Phase 4Completed
- Sponsor
- Amsterdam University Medical Center
- Start
- Nov 2024
- Modality
- Small Molecules
- Countries
- 1
01
Overview
Phase 4, open-label, single-arm trial of cholic acid in Bile Acid Synthesis Defects (BASD) and Zellweger spectrum disorder (PBD-ZSD), sponsored by Amsterdam University Medical Center. Primary endpoints: Suppression of endogenous bile acid synthesis, Adverse events and 1 more. Started Nov 2024; status: completed.
02
Drugs
cholic acid
03
Conditions
Bile Acid Synthesis Defects (BASD)Zellweger spectrum disorder (PBD-ZSD)
Beyond the preview
Go deeper on 2024-518652-23-00.
Study design, results and competitive context are available in the Gosset platform where reported.
Competitive context
Available in the Gosset platform where reported.
Bring the full picture into focus.
See how Gosset can support your research on 2024-518652-23-00.