Trial intelligence / Profile preview

Phase 2 open-label randomized study of bitopertin in erythropoietic protoporphyria

2025-000481-28Phase 2

Sponsor
Disc Medicine
Start
Mar 2026
Modality
Small Molecules
Countries
1
01

Overview

Phase 2, randomised, open-label trial of bitopertin in erythropoietic protoporphyria (EPP) (2 arms), sponsored by Disc Medicine. Primary endpoint: Percent change from baseline in whole blood metal-free PPIX levels.

02

Drugs

bitopertin
03

Conditions

erythropoietic protoporphyria (EPP)

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