Trial intelligence / Profile preview

Cannabidiol (Epidyolex) for behavioural problems in TSC, Sanfilippo and Fragile X syndrome: an N-of-1 series

2025-520846-31-00Phase 3Authorised

Sponsor
Amsterdam University Medical Center
Start
Oct 2025
Modality
Small Molecules
Countries
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Overview

Phase 3, randomised, double-blind trial of cannabidiol in tuberous sclerosis complex (TSC), Sanfilippo syndrome and Fragile X syndrome (FXS) (2 arms), sponsored by Amsterdam University Medical Center. Planned start Oct 2025; status: authorised.

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Drugs

cannabidiol
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Conditions

tuberous sclerosis complex (TSC)Sanfilippo syndromeFragile X syndrome (FXS)

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