Trial intelligence / Profile preview

ATL1102 in non-ambulatory Duchenne muscular dystrophy

ACTRN12618000970246Phase 2Completed

Sponsor
Percheron Therapeutics Ltd
Start
Aug 2018
Modality
Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Single-strand DNA → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics, Modified DNA Oligonucleotides → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

Phase 2, open-label, single-arm trial of avicursen in Duchenne muscular dystrophy (DMD), sponsored by Percheron Therapeutics Ltd. Primary endpoint: Safety and tolerability. Started Aug 2018; status: completed.

02

Drugs

avicursen
03

Conditions

Duchenne muscular dystrophy (DMD)

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