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Observational Study of Vamorolone vs Prednisone in Children with Duchenne Muscular Dystrophy
ChiCTR2600123519Phase 4Not yet recruiting
- Sponsor
- West China Second University Hospital
- Start
- Apr 2026
- Modality
- Orthosteric Ligands → Classical Binding Small Molecules → Small Molecules
- Countries
- 1
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Overview
Phase 4, open-label trial of vamorolone in Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD) (2 arms), sponsored by West China Second University Hospital. Primary endpoints: North Star Ambulatory Assessment (NSAA) score and Timed function test. Planned start Apr 2026; status: not yet recruiting.
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Drugs
vamorolone
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Conditions
Duchenne muscular dystrophy (DMD)Becker muscular dystrophy (BMD)
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