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Risdiplam in pre-symptomatic infants with SMA (China arm of FIREFISH-type study)
CTR20191488Phase 2Terminated
- Sponsor
- Roche
- Start
- Oct 2019
- Modality
- Small Molecules
- Countries
- 1
01
Overview
A Phase 2 trial of risdiplam in spinal muscular atrophy (SMA), sponsored by Roche. Started Oct 2019; status: terminated.
02
Drugs
risdiplam
03
Conditions
spinal muscular atrophy (SMA)
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