Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
Open-label single-arm 12‑month study of miglustat in Niemann–Pick disease type C in China
CTR20191637Phase 4Completed
- Sponsor
- Actelion Pharmaceuticals Ltd
- Start
- Aug 2019
- Modality
- Small Molecules
- Countries
- 1
01
Overview
A Phase 4 trial of miglustat in Niemann-Pick disease type C (NPC), sponsored by Actelion Pharmaceuticals Ltd. Started Aug 2019; status: completed.
02
Drugs
miglustat
03
Conditions
Niemann-Pick disease type C (NPC)
Beyond the preview
Go deeper on CTR20191637.
Study design, results and competitive context are available in the Gosset platform where reported.
Competitive context
Available in the Gosset platform where reported.
Bring the full picture into focus.
See how Gosset can support your research on CTR20191637.