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Phase III open-label single-arm crossover study of fitusiran prophylaxis in severe hemophilia A or B (with or without inhibitors)
CTR20230417Phase 3Active
- Sponsor
- Sanofi
- Start
- Jun 2023
- Modality
- Chemically Modified siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Conjugated siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
- Countries
- 1
01
Overview
Phase 3, open-label, single-arm trial of fitusiran in hemophilia A and hemophilia B (HB), sponsored by Sanofi. Primary endpoint: Annualized bleeding rate (ABR) during fitusiran prophylaxis main efficacy period. Started Jun 2023; status: active.
02
Drugs
fitusiran
03
Conditions
hemophilia Ahemophilia B (HB)
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