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Phase I/II open-label single-arm study of GC301 AAV injection in late-onset Pompe disease
CTR20241334Phase 2Active
- Sponsor
- GeneCradle
- Start
- Apr 2024
- Modality
- Gene Therapies
- Countries
- 1
01
Overview
A Phase 2 trial of gc301 in Pompe disease, sponsored by GeneCradle. Started Apr 2024; status: active.
02
Drugs
gc301
03
Conditions
Pompe disease
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