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ORION-19 inclisiran study in children with homozygous familial hypercholesterolemia
CTR20250166Phase 3Active
- Sponsor
- Novartis
- Start
- Aug 2025
- Modality
- Chemically Modified siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Conjugated siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, MicroRNA (miRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
- Countries
- 1
01
Overview
A Phase 3 trial of inclisiran in homozygous familial hypercholesterolemia (HoFH), sponsored by Novartis. Started Aug 2025; status: active.
02
Drugs
inclisiran
03
Conditions
homozygous familial hypercholesterolemia (HoFH)
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Competitive context
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