Trial intelligence / Profile preview

Phase 3 randomized open-label trial of intrathecal GC101 versus ongoing nusinersen in type 2 spinal muscular atrophy

CTR20251902Phase 3Active

Sponsor
GeneCradle
Start
Jun 2025
Modality
Cell Therapies
Countries
1
01

Overview

A Phase 3 trial of nolgileucel in spinal muscular atrophy type 2 (SMA2), sponsored by GeneCradle. Started Jun 2025; status: active.

02

Drugs

nolgileucel
03

Conditions

spinal muscular atrophy type 2 (SMA2)

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