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Long-term open-label extension study of VSA012 in paroxysmal nocturnal hemoglobinuria
CTR20261099Phase 2Active
- Sponsor
- Visirna Therapeutics
- Start
- Apr 2026
- Modality
- Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, MicroRNA (miRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
- Countries
- 1
01
Overview
A Phase 2 trial of VSA012 in paroxysmal nocturnal hemoglobinuria (PNH), sponsored by Visirna Therapeutics. Started Apr 2026; status: active.
02
Drugs
VSA012
03
Conditions
paroxysmal nocturnal hemoglobinuria (PNH)
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Competitive context
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