Trial intelligence / Profile preview

Intracerebroventricular VGN-R08b in pediatric type 3 Gaucher disease (Phase I/II)

CTR20261727Phase 2Active

Sponsor
T-MAXESTATE
Start
Apr 2026
Modality
Small Molecules, AAV Vectors → Viral Vectors → Gene Addition/Replacement → Gene Therapies
Countries
1
01

Overview

A Phase 2 trial of VGN-R08b in Gaucher disease type 3, sponsored by T-MAXESTATE. Started Apr 2026; status: active.

02

Drugs

VGN-R08b
03

Conditions

Gaucher disease type 3

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