Trial intelligence / Profile preview

Phase 3 trial of VSA012 versus eculizumab in complement inhibitor-naive PNH

CTR20263469Phase 3Active

Sponsor
Visirna Therapeutics
Start
Sep 2026
Modality
Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, MicroRNA (miRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

A Phase 3 trial of VSA012 in paroxysmal nocturnal hemoglobinuria (PNH), sponsored by Visirna Therapeutics. Started Sep 2026; status: active.

02

Drugs

VSA012
03

Conditions

paroxysmal nocturnal hemoglobinuria (PNH)

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