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OGT 918 (miglustat) in Niemann-Pick type C disease
ISRCTN26761144Phase 2Completed
- Sponsor
- Actelion Pharmaceuticals Ltd
- Start
- Mar 2003
- Modality
- Small Molecules
01
Overview
Phase 2, randomised, open-label trial of miglustat in Niemann-Pick disease type C (NPC) (3 arms), sponsored by Actelion Pharmaceuticals Ltd. Primary endpoint: Change from baseline in HSEM-alpha. Started Mar 2003; status: completed.
02
Drugs
miglustat
03
Conditions
Niemann-Pick disease type C (NPC)
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