Trial intelligence / Profile preview

ELEVATE-LTE long-term extension in Duchenne muscular dystrophy

ISRCTN31690502Phase 2Recruiting

Sponsor
Entrada Therapeutics
Start
Oct 2026
Modality
Gene Therapies, Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, MicroRNA (miRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
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Overview

Phase 2, open-label trial of ENTR-601-44 and ENTR-601-45 in Duchenne muscular dystrophy (DMD) (2 arms), sponsored by Entrada Therapeutics. Primary endpoint: Long-term safety and tolerability. Started Oct 2026; status: recruiting.

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Drugs

ENTR-601-44ENTR-601-45
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Conditions

Duchenne muscular dystrophy (DMD)

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