Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
Long-term Lamazym treatment in alpha-mannosidosis
ISRCTN96077718Phase 2Completed
- Sponsor
- Royal Manchester Children's Hospital
- Start
- Jun 2012
- Modality
- Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
01
Overview
Phase 2, open-label, single-arm trial of velmanase alfa in alpha-mannosidosis, sponsored by Royal Manchester Children's Hospital. Primary endpoints: Reduction of oligosaccharides in blood serum, Reduction of oligosaccharides in cerebrospinal fluid and 1 more. Started Jun 2012; status: completed.
02
Drugs
velmanase alfa
03
Conditions
alpha-mannosidosis
Beyond the preview
Go deeper on ISRCTN96077718.
Study design, results and competitive context are available in the Gosset platform where reported.
Competitive context
Available in the Gosset platform where reported.
Bring the full picture into focus.
See how Gosset can support your research on ISRCTN96077718.