Trial intelligence / Profile preview

Prospective observational study of emicizumab in infants with congenital hemophilia A

jRCT1031230264Active, not recruiting

Sponsor
Chugai Pharmaceutical Co., Ltd.
Start
Aug 2023
Modality
Bispecific Antibodies → Multispecific Antibodies → Engineered Antibody Formats → Antibody-Based Therapeutics, Monoclonal Antibodies → Antibody-Based Therapeutics
Countries
1
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Overview

Open-label, single-arm trial of emicizumab in hemophilia A, sponsored by Chugai Pharmaceutical Co., Ltd. Primary endpoint: Primary: Relationship between coagulation test parameters and plasma emicizumab levels (6–12 months). Started Aug 2023; status: active, not recruiting.

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Drugs

emicizumab
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Conditions

hemophilia A

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