Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
jRCT2011230040Phase 2Recruiting
Phase 2, randomised, double-blind trial in amyotrophic lateral sclerosis (ALS) comparing PTC857 with Placebo (2 arms). Primary endpoint: Change from baseline in ALS Functional Rating Scale-Revised (ALSFRS-R) in ITT1 after 24 weeks of treatment. Started Sep 2023; status: recruiting.
Beyond the preview
Study design, results and competitive context are available in the Gosset platform where reported.
Available in the Gosset platform where reported.
Available in the Gosset platform where reported.
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