Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
jRCT2011260022Phase 3Recruiting
Phase 3, randomised trial of BMN 333 in achondroplasia (ACH) (2 arms), sponsored by BioMarin Pharmaceutical Inc. Primary endpoints: Phase 2: Predicted Annualized Growth Velocity at Week 52 and Phase 3: Annualized Growth Velocity at Week 52. Started Jul 2026; status: recruiting.
Beyond the preview
Study design, results and competitive context are available in the Gosset platform where reported.
Available in the Gosset platform where reported.
Available in the Gosset platform where reported.
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