Trial intelligence / Profile preview

BMN 333 versus Vosoritide in Children with Achondroplasia

jRCT2011260022Phase 3Recruiting

Sponsor
BioMarin Pharmaceutical Inc.
Start
Jul 2026
Modality
Recombinant Proteins and Enzymes, Peptides
01

Overview

Phase 3, randomised trial of BMN 333 in achondroplasia (ACH) (2 arms), sponsored by BioMarin Pharmaceutical Inc. Primary endpoints: Phase 2: Predicted Annualized Growth Velocity at Week 52 and Phase 3: Annualized Growth Velocity at Week 52. Started Jul 2026; status: recruiting.

02

Drugs

BMN 333
03

Conditions

achondroplasia (ACH)

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