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ACCESS-EXT: Long-term Open-Label Extension of Pozelimab + Cemdisiran in PNH
jRCT2031230013Recruiting
- Sponsor
- Regeneron Pharmaceuticals
- Start
- Jan 2024
- Modality
- Monoclonal Antibodies → Antibody-Based Therapeutics, Recombinant Proteins and Enzymes, Chemically Modified siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
01
Overview
Open-label trial of pozelimab and cemdisiran in paroxysmal nocturnal hemoglobinuria (PNH) (2 arms), sponsored by Regeneron Pharmaceuticals. Primary endpoints: Incidence of treatment-emergent serious adverse events (SAEs), Severity of treatment-emergent SAEs and 5 more. Started Jan 2024; status: recruiting.
02
Drugs
pozelimabcemdisiran
03
Conditions
paroxysmal nocturnal hemoglobinuria (PNH)
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