Trial intelligence / Profile preview

Gefurulimab PK/PD, safety and efficacy in pediatric AChR+ generalized myasthenia gravis

jRCT2031250602Recruiting

Sponsor
Alexion Pharmaceuticals
Start
Jan 2026
Modality
Nanobodies (VHH) → Antibody Fragments → Engineered Antibody Formats → Antibody-Based Therapeutics, Bispecific Antibodies → Multispecific Antibodies → Engineered Antibody Formats → Antibody-Based Therapeutics, Fc-Fusion Proteins → Carrier/Scaffold Proteins → Recombinant Proteins and Enzymes
01

Overview

Open-label, single-arm trial of gefurulimab in generalized myasthenia gravis (gMG), sponsored by Alexion Pharmaceuticals. Primary endpoints: Pharmacokinetics of gefurulimab and Pharmacodynamics of gefurulimab. Started Jan 2026; status: recruiting.

02

Drugs

gefurulimab
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Conditions

generalized myasthenia gravis (gMG)

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