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Phase 1 extension study of NS-035 in Fukuyama-type congenital muscular dystrophy

jRCT2031250857Phase 1Recruiting

Sponsor
Nippon Shinyaku
Start
Apr 2026
Modality
Small Molecules
Countries
1
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Overview

Phase 1, open-label, single-arm trial of NS-035 in Fukuyama congenital muscular dystrophy (FCMD), sponsored by Nippon Shinyaku. Primary endpoints: Adverse events, Physical and neurological examination and 11 more. Started Apr 2026; status: recruiting.

02

Drugs

NS-035
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Conditions

Fukuyama congenital muscular dystrophy (FCMD)

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