Trial intelligence / Profile preview

Phase 1/2 multiple-dose study of NS-050/NCNP-03 in boys with Duchenne muscular dystrophy

jRCT2041240060Phase 2Recruiting

Sponsor
NS Pharma, Inc.
Start
Sep 2024
Modality
Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Single-strand DNA → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics, Modified DNA Oligonucleotides → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics
01

Overview

Phase 2, randomised trial of NS-050 in Duchenne muscular dystrophy (DMD) (3 arms), sponsored by NS Pharma, Inc. Primary endpoint: Biceps brachii muscle dystrophin protein by Western blot. Started Sep 2024; status: recruiting.

02

Drugs

NS-050
03

Conditions

Duchenne muscular dystrophy (DMD)

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