Trial intelligence / Profile preview

Phase 3 study of vosoritide in children with hypochondroplasia

jRCT2051240179Phase 3Completed

Sponsor
BioMarin Pharmaceutical Inc.
Start
Dec 2024
Modality
Recombinant Proteins and Enzymes, Peptides
01

Overview

Phase 3, randomised, double-blind trial in hypochondroplasia (HCH) comparing Vosoritide with Placebo (2 arms). Primary endpoint: Change from baseline in annualized growth velocity at Week 52 versus placebo. Started Dec 2024; status: completed.

02

Drugs

vosoritide
03

Conditions

hypochondroplasia (HCH)

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