Trial intelligence / Profile preview

ACT-EARLY: Acoramidis for Prevention of Transthyretin Amyloidosis in Young At-Risk Adults

jRCT2071250116Phase 3Recruiting

Sponsor
Eidos Therapeutics
Start
Dec 2025
Modality
Small Molecules
01

Overview

Phase 3, randomised, double-blind trial in transthyretin amyloidosis (ATTR) comparing Acoramidis with Placebo (2 arms). Primary endpoint: Time to development of ATTR (ATTR-CM or ATTR-PN). Started Dec 2025; status: recruiting.

02

Drugs

acoramidis
03

Conditions

transthyretin amyloidosis (ATTR)

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