Trial intelligence / Profile preview

Risdiplam in non-ambulant type 2 and 3 spinal muscular atrophy (Japan, double-blind, placebo-controlled)

jRCT2080223666Phase 2Completed

Sponsor
Chugai Pharmaceutical Co., Ltd.
Start
Oct 2017
Modality
Small Molecules
01

Overview

Phase 2, randomised, double-blind trial in spinal muscular atrophy type 2 (SMA2) and Spinal muscular atrophy type 3 (SMA3) comparing Risdiplam with Placebo (2 arms). Started Oct 2017; status: completed.

02

Drugs

risdiplam
03

Conditions

spinal muscular atrophy type 2 (SMA2)Spinal muscular atrophy type 3 (SMA3)

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