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MRCD Study of SPP-004 in pediatric mitochondrial disease
jRCT2091220200Completed
- Sponsor
- Saitama Medical University Hospital
- Start
- Dec 2014
- Modality
- Small Molecules
- Countries
- 1
01
Overview
Randomised, double-blind trial in Mitochondriopathy and electron transport chain deficiencies comparing SPP-004 active treatment with Placebo comparator (2 arms). Primary endpoint: Newcastle Paediatric Mitochondrial Disease Scale (NPMDS) Sections I–III. Started Dec 2014; status: completed.
02
Drugs
5-aminolevulinic acid hydrochloride + sodium ferrous citrate
03
Conditions
Mitochondriopathyelectron transport chain deficiencies
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