Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
Triheptanoin in citrin deficiency
jRCTs031230755Recruiting
- Sponsor
- Ultragenyx Pharmaceutical Inc.
- Start
- May 2024
- Modality
- Small Molecules
- Countries
- 1
01
Overview
Open-label, single-arm trial of triheptanoin in citrin deficiency, sponsored by Ultragenyx Pharmaceutical Inc. Primary endpoint: Safety (adverse events during treatment). Started May 2024; status: recruiting.
02
Drugs
triheptanoin
03
Conditions
citrin deficiency
Beyond the preview
Go deeper on jRCTs031230755.
Study design, results and competitive context are available in the Gosset platform where reported.
Competitive context
Available in the Gosset platform where reported.
Bring the full picture into focus.
See how Gosset can support your research on jRCTs031230755.