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AAV-hAADC-2 Gene Therapy for AADC Deficiency
jRCTs033180309Completed
- Sponsor
- Japan Agency for Medical Research and Development
- Start
- Jun 2015
- Modality
- Gene Therapies
- Countries
- 1
01
Overview
Open-label, single-arm trial of ezaladcigene resoparvovec in Aromatic L-amino acid decarboxylase deficiency (AADC), sponsored by Japan Agency for Medical Research and Development. Started Jun 2015; status: completed.
02
Drugs
ezaladcigene resoparvovec
03
Conditions
Aromatic L-amino acid decarboxylase deficiency (AADC)
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