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Carglumic acid in late-onset ornithine transcarbamylase deficiency
jRCTs041190055Completed
- Sponsor
- Recordati Rare Diseases
- Start
- Jul 2019
- Modality
- Small Molecules
- Countries
- 1
01
Overview
Open-label, single-arm trial of carglumic acid in ornithine transcarbamylase deficiency, sponsored by Recordati Rare Diseases. Primary endpoint: change of blood glutamine levels. Started Jul 2019; status: completed.
02
Drugs
carglumic acid
03
Conditions
ornithine transcarbamylase deficiency
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