Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
Folinic acid replacement therapy for inherited GPI deficiency
jRCTs051180113Completed
- Sponsor
- Japan Research Foundation for Clinical Pharmacology
- Start
- Nov 2021
- Modality
- Orthosteric Ligands → Classical Binding Small Molecules → Small Molecules
- Countries
- 1
01
Overview
Open-label, single-arm trial of folinic acid in congenital glycosylphosphatidylinositol deficiency (IGD), sponsored by Japan Research Foundation for Clinical Pharmacology. Primary endpoint: Seizure frequency. Started Nov 2021; status: completed.
02
Drugs
folinic acid
03
Conditions
congenital glycosylphosphatidylinositol deficiency (IGD)
Beyond the preview
Go deeper on jRCTs051180113.
Study design, results and competitive context are available in the Gosset platform where reported.
Competitive context
Available in the Gosset platform where reported.
Bring the full picture into focus.
See how Gosset can support your research on jRCTs051180113.