Trial intelligence / Profile preview

Open-label phase 3 study of lumasiran in infants and young children with primary hyperoxaluria type 1

MOH_2019-03-03_006004Phase 3Completed

Sponsor
Alnylam Pharmaceuticals
Start
Feb 2019
Modality
Chemically Modified siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Conjugated siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

Phase 3, open-label, single-arm trial of lumasiran in Primary Hyperoxaluria Type 1 (PH1), sponsored by Alnylam Pharmaceuticals. Primary endpoint: Change in urinary oxalate excretion. Started Feb 2019; status: completed.

02

Drugs

lumasiran
03

Conditions

Primary Hyperoxaluria Type 1 (PH1)

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