Trial intelligence / Profile preview

Glycerol phenylbutyrate in children with MCT8 mutation (Allan-Herndon-Dudley syndrome)

MOH_2019-11-17_007491Phase 4Not yet recruiting

Sponsor
פרופ. אמנון צונג
Start
Nov 2019
Modality
Small Molecules
Countries
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Overview

Phase 4, open-label, single-arm trial of sodium phenylbutyrate in Allan-Herndon-Dudley syndrome (AHDS), sponsored by פרופ. אמנון צונג. Planned start Nov 2019; status: not yet recruiting.

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Drugs

sodium phenylbutyrate
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Conditions

Allan-Herndon-Dudley syndrome (AHDS)

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