Trial intelligence / Profile preview

Phase 1/2 open-label dose-ranging study of PBKR03 in early infantile Krabbe disease

MOH_2021-12-19_010490Phase 2Completed

Sponsor
Passage Bio
Start
May 2021
Modality
Gene Therapies
Countries
1
01

Overview

Phase 2, open-label trial of PBKR03 in Krabbe disease (5 arms), sponsored by Passage Bio. Primary endpoint: Safety and tolerability of PBKR03. Started May 2021; status: completed.

02

Drugs

PBKR03
03

Conditions

Krabbe disease

Beyond the preview

Go deeper on MOH_2021-12-19_010490.

Study design, results and competitive context are available in the Gosset platform where reported.

Study design & results

Available in the Gosset platform where reported.

Competitive context

Available in the Gosset platform where reported.

Bring the full picture into focus.

See how Gosset can support your research on MOH_2021-12-19_010490.

Gosset Free

Get started with Gosset.

Enter your corporate email.

Work email preferred.

Book a call