Trial intelligence / Profile preview

Phase 3 FLT201 gene therapy study in adults with Gaucher disease type 1

MOH_2026-02-23_015679Phase 3Not yet recruiting

Sponsor
Spur Therapeutics
Start
Feb 2026
Modality
Viral Vectors → Gene Addition/Replacement → Gene Therapies
Countries
1
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Overview

Phase 3, open-label, single-arm trial of avigbagene parvec in Gaucher disease type 1 (GD1), sponsored by Spur Therapeutics. Primary endpoint: Stable hemoglobin concentration at week 52. Planned start Feb 2026; status: not yet recruiting.

02

Drugs

avigbagene parvec
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Conditions

Gaucher disease type 1 (GD1)

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