Trial intelligence / Profile preview

Safety of Afegostat Tartrate in Type 1 Gaucher Disease

NCT00446550Phase 2Completed

Sponsor
Amicus Therapeutics
Start
Jun 2008
Primary completion
Aug 2009
Modality
Small Molecules
Countries
4
01

Overview

A Phase 2 trial of Afegostat in Gaucher disease type 1 (GD1), sponsored by Amicus Therapeutics. Started Jun 2008; status: completed.

02

Drugs

Afegostat
03

Conditions

Gaucher disease type 1 (GD1)

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