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SA-ER in GNE Myopathy
NCT01517880Phase 2Completed
- Sponsor
- Ultragenyx Pharmaceutical Inc.
- Start
- May 2012
- Primary completion
- Nov 2013
- Modality
- Small Molecules
- Countries
- 2
01
Overview
A Phase 2 trial of aceneuramic acid in GNE myopathy (HIBM), sponsored by Ultragenyx Pharmaceutical Inc.. Started May 2012; status: completed.
02
Drugs
aceneuramic acid
03
Conditions
GNE myopathy (HIBM)
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