Trial intelligence / Profile preview

Kuvan long-term neurocognitive outcomes in children with PKU

NCT01965912Phase 4Completed

Sponsor
BioMarin Pharmaceutical
Start
Oct 2013
Primary completion
Jan 2023
Modality
Allosteric Modulators, Metabolically Activated Prodrugs
Countries
4
01

Overview

A Phase 4 trial of sapropterin in phenylketonuria (PKU), sponsored by BioMarin Pharmaceutical. Started Oct 2013; status: completed.

02

Drugs

sapropterin
03

Conditions

phenylketonuria (PKU)

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