Trial intelligence / Profile preview

rAAV1.CMV.huFollistatin344 in Duchenne Muscular Dystrophy

NCT02354781Phase 2Completed

Start
Jan 2015
Primary completion
Nov 2017
Modality
Gene Editing, Gene Silencing, Gene Addition/Replacement
Countries
1
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Overview

Phase 2, open-label, single-arm trial of rAAV1.CMV.huFollistatin344 in Duchenne muscular dystrophy (DMD). Primary endpoint: Dose Limiting Toxicity Adverse Events at 2 years. Started Jan 2015; status: completed.

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Drugs

rAAV1.CMV.huFollistatin344
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Conditions

Duchenne muscular dystrophy (DMD)

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