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Pilot Study of AVR-RD-01 Gene Therapy for Fabry Disease
NCT02800070Phase 1Completed
- Sponsor
- University Health Network
- Start
- Jul 2016
- Primary completion
- Apr 2024
- Modality
- Gene Editing, Gene Silencing, Stem Cell Therapies
- Countries
- 1
01
Overview
Phase 1, open-label, single-arm trial of AVR-RD-01 in Fabry disease (FD), sponsored by University Health Network. Primary endpoint: Number of Participants With Abnormal Laboratory Values and/or Adverse Events That Are Related to Treatment at 5 years. Started Jul 2016; status: completed.
02
Drugs
AVR-RD-01
03
Conditions
Fabry disease (FD)
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