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The Effect of Triheptanoin in Adults With Mc Ardle Disease
NCT02919631Phase 2Completed
- Sponsor
- Inserm
- Start
- Nov 2016
- Primary completion
- Jun 2017
- Modality
- SLNs, Nanostructured Lipid Carriers, Small Molecules
- Countries
- 1
01
Overview
Phase 2, randomised, double-blind trial in Glycogen storage disease type 5 (GSD5) comparing triheptanoin with placebo oil (2 arms). Primary endpoint: Change in heart rate during constant load cycling exercise at Day 28. Started Nov 2016; status: completed.
02
Drugs
triheptanoin
03
Conditions
Glycogen storage disease type 5 (GSD5)
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