Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
NCT03201627Phase 1Unknown
Phase 1, open-label, single-arm trial of lithium carbonate in Niemann-Pick disease type C1 (NPC1), sponsored by Xinhua Hospital. Primary endpoint: NPC Clinical Severity Score at 52 weeks. Status: unknown.
Beyond the preview
Study design, results and competitive context are available in the Gosset platform where reported.
Available in the Gosset platform where reported.
Available in the Gosset platform where reported.
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