Trial intelligence / Profile preview

Ataluren Dystrophin Assessment in nmDMD

NCT03796637Phase 2Completed

Sponsor
PTC Therapeutics, Inc.
Start
Apr 2019
Primary completion
Jun 2019
Modality
Small Molecules
Countries
1
01

Overview

Phase 2, open-label, single-arm trial of ataluren in Duchenne muscular dystrophy (DMD), sponsored by PTC Therapeutics, Inc. Primary endpoint: Mean Dystrophin Levels as Measured by Electrochemiluminescence (ECL) at Day 1. Started Apr 2019; status: completed.

02

Drugs

ataluren
03

Conditions

Duchenne muscular dystrophy (DMD)

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